Hereditary Amyloidosis is a very rare disorder. It’s a genetic disorder where the gene is autosomal dominant, meaning it’s passed from parent to child at a 50% rate. And most people who get the gene have the disease or develop the disease.
There is currently an avalanche of new therapies in rare, neurologic disease occurring in the world, including Canada. This is the beginning of a revolution in therapy. Patients who have never had therapies for their diseases, now have the opportunity to be treated, and in some cases cured of the symptoms of the disease they carry.